Novel CFTR modulator combinations maximize rescue of G85E and N1303K in rectal organoids
Pseudomonas aeruginosa in cystic fibrosis patients with c.1652G›A (G551D)‐CFTR treated with ivacaftor—Changes in microbiological parameters - Millar - 2018 - Journal of Clinical Pharmacy and Therapeutics - Wiley Online Library
PDF) Ivacaftor in cystic fibrosis adults: Czech experience with six years of follow-up
Filas de registro e pós-registro têm redução - cosmetovigilancia - Anvisa
Pseudomonas aeruginosa in cystic fibrosis patients with c.1652G›A (G551D)‐CFTR treated with ivacaftor—Changes in microbiological parameters - Millar - 2018 - Journal of Clinical Pharmacy and Therapeutics - Wiley Online Library
Transformative therapies for rare CFTR missense alleles - ScienceDirect
PDF) Human epididymis protein 4 (HE4) levels inversely correlate with lung function improvement (delta FEV1) in cystic fibrosis patients receiving ivacaftor treatment